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Title : Familial lecithin:cholesterol acyltransferase deficiency: First-in-human treatment with enzyme replacement - Shamburek_2016_J.Clin.Lipidol_10_356 |
Author(s) : Shamburek RD , Bakker-Arkema R , Auerbach BJ , Krause BR , Homan R , Amar MJ , Freeman LA , Remaley AT |
Ref : J Clin Lipidol , 10 :356 , 2016 |
Abstract : Shamburek_2016_J.Clin.Lipidol_10_356 |
ESTHER : Shamburek_2016_J.Clin.Lipidol_10_356 |
PubMedSearch : Shamburek_2016_J.Clin.Lipidol_10_356 |
PubMedID: 27055967 |
Gene_locus related to this paper: human-LCAT |
Title : Safety and Tolerability of ACP-501, a Recombinant Human Lecithin:Cholesterol Acyltransferase, in a Phase 1 Single-Dose Escalation Study - Shamburek_2016_Circ.Res_118_73 |
Author(s) : Shamburek RD , Bakker-Arkema R , Shamburek AM , Freeman LA , Amar MJ , Auerbach B , Krause BR , Homan R , Adelman SJ , Collins HL , Sampson M , Wolska A , Remaley AT |
Ref : Circulation Research , 118 :73 , 2016 |
Abstract : Shamburek_2016_Circ.Res_118_73 |
ESTHER : Shamburek_2016_Circ.Res_118_73 |
PubMedSearch : Shamburek_2016_Circ.Res_118_73 |
PubMedID: 26628614 |
Gene_locus related to this paper: human-LCAT |