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Title : Sebelipase alfa over 52 weeks reduces serum transaminases, liver volume and improves serum lipids in patients with lysosomal acid lipase deficiency - Valayannopoulos_2014_J.Hepatol_61_1135 |
Author(s) : Valayannopoulos V , Malinova V , Honzik T , Balwani M , Breen C , Deegan PB , Enns GM , Jones SA , Kane JP , Stock EO , Tripuraneni R , Eckert S , Schneider E , Hamilton G , Middleton MS , Sirlin C , Kessler B , Bourdon C , Boyadjiev SA , Sharma R , Twelves C , Whitley CB , Quinn AG |
Ref : Journal of Hepatology , 61 :1135 , 2014 |
Abstract : Valayannopoulos_2014_J.Hepatol_61_1135 |
ESTHER : Valayannopoulos_2014_J.Hepatol_61_1135 |
PubMedSearch : Valayannopoulos_2014_J.Hepatol_61_1135 |
PubMedID: 24993530 |
Gene_locus related to this paper: human-LIPA |