Bigger BW

References (1)

Title : Enzyme replacement therapy and hematopoietic stem cell transplant: a new paradigm of treatment in Wolman disease - Potter_2021_Orphanet.J.Rare.Dis_16_235

Author(s) : Potter JE , Petts G , Ghosh A , White FJ , Kinsella JL , Hughes S , Roberts J , Hodgkinson A , Brammeier K , Church H , Merrigan C , Hughes J , Evans P , Campbell H , Bonney D , Newman WG , Bigger BW , Broomfield A , Jones SA , Wynn RF

Ref : Orphanet J Rare Dis , 16 :235 , 2021

Abstract :

PubMedSearch : Potter_2021_Orphanet.J.Rare.Dis_16_235

PubMedID: 34020687

Gene_locus related to this paper: human-LIPA

Bigger BW

References (1)

1. Enzyme replacement therapy and hematopoietic stem cell transplant: a new paradigm of treatment in Wolman disease - Potter_2021_Orphanet.J.Rare.Dis_16_235