Title : Breaking the chains of lipoprotein lipase deficiency: A pediatric perspective on the efficacy and safety of Volanesorsen - den Hollander_2024_Mol.Genet.Metab_142_108347 |
Author(s) : den Hollander B , Brands MM , Nijhuis IJM , Doude van Troostwijk L , van Essen P , Hofsteenge AH , Koot BG , Muller AR , Tseng LA , Stroes ESG , van de Ven PM , Wiegman A , van Karnebeek CDM |
Ref : Mol Genet Metab , 142 :108347 , 2024 |
PubMedID: 38401382 |