| Title : Phase 1 Trials of PNPLA3 siRNA in I148M Homozygous Patients with MAFLD - |
| Author(s) : Fabbrini E , Rady B , Koshkina A , Jeon JY , Ayyar VS , Gargano C , DiProspero N , Wendel S , Hegge J , Hamilton H , Ding ZM , Afrazi M , Nicholas A , Pei T , Nakano M , Ouchi S , Saito Y , Yamashita A , Tamamura R , Salazar H , Shapiro C , Yoshihara T , Yonemura T , Inoue S , Matsuoka O , Erion M , Pocai A , Makimura H |
| Ref : N Engl J Med , 391 :475 , 2024 |
| PubMedID: 39083780 |
| Title : Phase 1 Trials of PNPLA3 siRNA in I148M Homozygous Patients with MAFLD - |
| Author(s) : Fabbrini E , Rady B , Koshkina A , Jeon JY , Ayyar VS , Gargano C , DiProspero N , Wendel S , Hegge J , Hamilton H , Ding ZM , Afrazi M , Nicholas A , Pei T , Nakano M , Ouchi S , Saito Y , Yamashita A , Tamamura R , Salazar H , Shapiro C , Yoshihara T , Yonemura T , Inoue S , Matsuoka O , Erion M , Pocai A , Makimura H |
| Ref : N Engl J Med , 391 :475 , 2024 |
| PubMedID: 39083780 |
| Title : Phase 1 Trials of PNPLA3 siRNA in I148M Homozygous Patients with MAFLD - |
| Author(s) : Fabbrini E , Rady B , Koshkina A , Jeon JY , Ayyar VS , Gargano C , DiProspero N , Wendel S , Hegge J , Hamilton H , Ding ZM , Afrazi M , Nicholas A , Pei T , Nakano M , Ouchi S , Saito Y , Yamashita A , Tamamura R , Salazar H , Shapiro C , Yoshihara T , Yonemura T , Inoue S , Matsuoka O , Erion M , Pocai A , Makimura H |
| Ref : N Engl J Med , 391 :475 , 2024 |
| PubMedID: 39083780 |
| Title : Glycosylphosphatidylinositol-anchored high-density lipoprotein-binding protein 1 plays a critical role in the lipolytic processing of chylomicrons - Beigneux_2007_Cell.Metab_5_279 |
| Author(s) : Beigneux AP , Davies BS , Gin P , Weinstein MM , Farber E , Qiao X , Peale F , Bunting S , Walzem RL , Wong JS , Blaner WS , Ding ZM , Melford K , Wongsiriroj N , Shu X , de Sauvage F , Ryan RO , Fong LG , Bensadoun A , Young SG |
| Ref : Cell Metab , 5 :279 , 2007 |
| Abstract : |
| PubMedSearch : Beigneux_2007_Cell.Metab_5_279 |
| PubMedID: 17403372 |
| Title : Glycosylphosphatidylinositol-anchored high-density lipoprotein-binding protein 1 plays a critical role in the lipolytic processing of chylomicrons - Beigneux_2007_Cell.Metab_5_279 |
| Author(s) : Beigneux AP , Davies BS , Gin P , Weinstein MM , Farber E , Qiao X , Peale F , Bunting S , Walzem RL , Wong JS , Blaner WS , Ding ZM , Melford K , Wongsiriroj N , Shu X , de Sauvage F , Ryan RO , Fong LG , Bensadoun A , Young SG |
| Ref : Cell Metab , 5 :279 , 2007 |
| Abstract : |
| PubMedSearch : Beigneux_2007_Cell.Metab_5_279 |
| PubMedID: 17403372 |
| Title : Glycosylphosphatidylinositol-anchored high-density lipoprotein-binding protein 1 plays a critical role in the lipolytic processing of chylomicrons - Beigneux_2007_Cell.Metab_5_279 |
| Author(s) : Beigneux AP , Davies BS , Gin P , Weinstein MM , Farber E , Qiao X , Peale F , Bunting S , Walzem RL , Wong JS , Blaner WS , Ding ZM , Melford K , Wongsiriroj N , Shu X , de Sauvage F , Ryan RO , Fong LG , Bensadoun A , Young SG |
| Ref : Cell Metab , 5 :279 , 2007 |
| Abstract : |
| PubMedSearch : Beigneux_2007_Cell.Metab_5_279 |
| PubMedID: 17403372 |