Title : Development of an antisense oligonucleotide-mediated exon skipping therapeutic strategy for Mucolipidosis II: validation at RNA level - Matos_2020_Hum.Gene.Ther__ |
Author(s) : Matos L , Vilela R , Rocha M , Santos JI , Coutinho MF , Gaspar P , Prata MJ , Alves S |
Ref : Hum Gene Therapy , : , 2020 |
Abstract : Matos_2020_Hum.Gene.Ther__ |
ESTHER : Matos_2020_Hum.Gene.Ther__ |
PubMedSearch : Matos_2020_Hum.Gene.Ther__ |
PubMedID: 32283951 |