| Title : Development of an antisense oligonucleotide-mediated exon skipping therapeutic strategy for Mucolipidosis II: validation at RNA level - Matos_2020_Hum.Gene.Ther__ |
| Author(s) : Matos L , Vilela R , Rocha M , Santos JI , Coutinho MF , Gaspar P , Prata MJ , Alves S |
| Ref : Hum Gene Therapy , : , 2020 |
| Abstract : Matos_2020_Hum.Gene.Ther__ |
| ESTHER : Matos_2020_Hum.Gene.Ther__ |
| PubMedSearch : Matos_2020_Hum.Gene.Ther__ |
| PubMedID: 32283951 |