Title : High-Dose ERT, Rituximab, and Early HSCT in an Infant with Wolman's Disease - Eskandari_2024_N.Engl.J.Med_390_623 |
Author(s) :
Eskandari SK , Revenich EGM , Pot DJ , de Boer F , Bierings M , van Spronsen FJ , van Hasselt PM , Lindemans CA , Lubout CMA |
Ref :
N Engl J Med , 390 :623 , 2024 |
Abstract : Eskandari_2024_N.Engl.J.Med_390_623 |
ESTHER : Eskandari_2024_N.Engl.J.Med_390_623 |
PubMedSearch : Eskandari_2024_N.Engl.J.Med_390_623 |
PubMedID: 38354141 |
Gene_locus related to this paper:
human-LIPA |