Title : High-Dose ERT, Rituximab, and Early HSCT in an Infant with Wolman's Disease - Eskandari_2024_N.Engl.J.Med_390_623 |
Author(s) : Eskandari SK , Revenich EGM , Pot DJ , de Boer F , Bierings M , van Spronsen FJ , van Hasselt PM , Lindemans CA , Lubout CMA |
Ref : N Engl J Med , 390 :623 , 2024 |
Abstract : Eskandari_2024_N.Engl.J.Med_390_623 |
ESTHER : Eskandari_2024_N.Engl.J.Med_390_623 |
PubMedSearch : Eskandari_2024_N.Engl.J.Med_390_623 |
PubMedID: 38354141 |
Gene_locus related to this paper: human-LIPA |
Gene_locus related to this paper: human-LIPA |
Eskandari SK, Revenich EGM, Pot DJ, de Boer F, Bierings M, van Spronsen FJ, van Hasselt PM, Lindemans CA, Lubout CMA (2024)
High-Dose ERT, Rituximab, and Early HSCT in an Infant with Wolman's Disease
N Engl J Med
390 :623
Eskandari SK, Revenich EGM, Pot DJ, de Boer F, Bierings M, van Spronsen FJ, van Hasselt PM, Lindemans CA, Lubout CMA (2024)
N Engl J Med
390 :623