Title : Safety and efficacy of mTOR inhibitor treatment in patients with tuberous sclerosis complex under 2 years of age - a multicenter retrospective study - Saffari_2019_Orphanet.J.Rare.Dis_14_96 |
Author(s) : Saffari A , Brosse I , Wiemer-Kruel A , Wilken B , Kreuzaler P , Hahn A , Bernhard MK , van Tilburg CM , Hoffmann GF , Gorenflo M , Hethey S , Kaiser O , Kolker S , Wagner R , Witt O , Merkenschlager A , Mockel A , Roser T , Schlump JU , Serfling A , Spiegler J , Milde T , Ziegler A , Syrbe S |
Ref : Orphanet J Rare Dis , 14 :96 , 2019 |
Abstract : Saffari_2019_Orphanet.J.Rare.Dis_14_96 |
ESTHER : Saffari_2019_Orphanet.J.Rare.Dis_14_96 |
PubMedSearch : Saffari_2019_Orphanet.J.Rare.Dis_14_96 |
PubMedID: 31053163 |
Saffari A, Brosse I, Wiemer-Kruel A, Wilken B, Kreuzaler P, Hahn A, Bernhard MK, van Tilburg CM, Hoffmann GF, Gorenflo M, Hethey S, Kaiser O, Kolker S, Wagner R, Witt O, Merkenschlager A, Mockel A, Roser T, Schlump JU, Serfling A, Spiegler J, Milde T, Ziegler A, Syrbe S (2019)
Safety and efficacy of mTOR inhibitor treatment in patients with tuberous sclerosis complex under 2 years of age - a multicenter retrospective study
Orphanet J Rare Dis
14 :96
Saffari A, Brosse I, Wiemer-Kruel A, Wilken B, Kreuzaler P, Hahn A, Bernhard MK, van Tilburg CM, Hoffmann GF, Gorenflo M, Hethey S, Kaiser O, Kolker S, Wagner R, Witt O, Merkenschlager A, Mockel A, Roser T, Schlump JU, Serfling A, Spiegler J, Milde T, Ziegler A, Syrbe S (2019)
Orphanet J Rare Dis
14 :96