Saffari_2019_Orphanet.J.Rare.Dis_14_96

Reference

Title : Safety and efficacy of mTOR inhibitor treatment in patients with tuberous sclerosis complex under 2 years of age - a multicenter retrospective study - Saffari_2019_Orphanet.J.Rare.Dis_14_96
Author(s) : Saffari A , Brosse I , Wiemer-Kruel A , Wilken B , Kreuzaler P , Hahn A , Bernhard MK , van Tilburg CM , Hoffmann GF , Gorenflo M , Hethey S , Kaiser O , Kolker S , Wagner R , Witt O , Merkenschlager A , Mockel A , Roser T , Schlump JU , Serfling A , Spiegler J , Milde T , Ziegler A , Syrbe S
Ref : Orphanet J Rare Dis , 14 :96 , 2019
Abstract : Saffari_2019_Orphanet.J.Rare.Dis_14_96
ESTHER : Saffari_2019_Orphanet.J.Rare.Dis_14_96
PubMedSearch : Saffari_2019_Orphanet.J.Rare.Dis_14_96
PubMedID: 31053163

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Saffari A, Brosse I, Wiemer-Kruel A, Wilken B, Kreuzaler P, Hahn A, Bernhard MK, van Tilburg CM, Hoffmann GF, Gorenflo M, Hethey S, Kaiser O, Kolker S, Wagner R, Witt O, Merkenschlager A, Mockel A, Roser T, Schlump JU, Serfling A, Spiegler J, Milde T, Ziegler A, Syrbe S (2019)
Safety and efficacy of mTOR inhibitor treatment in patients with tuberous sclerosis complex under 2 years of age - a multicenter retrospective study
Orphanet J Rare Dis 14 :96

Saffari A, Brosse I, Wiemer-Kruel A, Wilken B, Kreuzaler P, Hahn A, Bernhard MK, van Tilburg CM, Hoffmann GF, Gorenflo M, Hethey S, Kaiser O, Kolker S, Wagner R, Witt O, Merkenschlager A, Mockel A, Roser T, Schlump JU, Serfling A, Spiegler J, Milde T, Ziegler A, Syrbe S (2019)
Orphanet J Rare Dis 14 :96