| Title : Synergistic effects of treating the spinal cord and brain in CLN1 disease - Shyng_2017_Proc.Natl.Acad.Sci.U.S.A_114_E5920 |
| Author(s) : Shyng C , Nelvagal HR , Dearborn JT , Tyynela J , Schmidt RE , Sands MS , Cooper JD |
| Ref : Proc Natl Acad Sci U S A , 114 :E5920 , 2017 |
| Abstract : |
| PubMedSearch : Shyng_2017_Proc.Natl.Acad.Sci.U.S.A_114_E5920 |
| PubMedID: 28673981 |
| Gene_locus related to this paper: mouse-ppt |
| Title : Intrathecal enzyme replacement therapy improves motor function and survival in a preclinical mouse model of infantile neuronal ceroid lipofuscinosis - Lu_2015_Mol.Genet.Metab_116_98 |
| Author(s) : Lu JY , Nelvagal HR , Wang L , Birnbaum SG , Cooper JD , Hofmann SL |
| Ref : Mol Genet Metab , 116 :98 , 2015 |
| Abstract : |
| PubMedSearch : Lu_2015_Mol.Genet.Metab_116_98 |
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| Gene_locus related to this paper: mouse-ppt |
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| Author(s) : Hawkins-Salsbury JA , Cooper JD , Sands MS |
| Ref : Biochimica & Biophysica Acta , 1832 :1906 , 2013 |
| Abstract : |
| PubMedSearch : Hawkins-Salsbury_2013_Biochim.Biophys.Acta_1832_1906 |
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| Title : Intravenous high-dose enzyme replacement therapy with recombinant palmitoyl-protein thioesterase reduces visceral lysosomal storage and modestly prolongs survival in a preclinical mouse model of infantile neuronal ceroid lipofuscinosis - Hu_2012_Mol.Genet.Metab_107_213 |
| Author(s) : Hu J , Lu JY , Wong AM , Hynan LS , Birnbaum SG , Yilmaz DS , Streit BM , Lenartowicz EM , Thompson TC , Cooper JD , Hofmann SL |
| Ref : Mol Genet Metab , 107 :213 , 2012 |
| Abstract : |
| PubMedSearch : Hu_2012_Mol.Genet.Metab_107_213 |
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| Gene_locus related to this paper: mouse-ppt |
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| Author(s) : Macauley SL , Roberts MS , Wong AM , McSloy F , Reddy AS , Cooper JD , Sands MS |
| Ref : Annals of Neurology , 71 :797 , 2012 |
| Abstract : |
| PubMedSearch : Macauley_2012_Ann.Neurol_71_797 |
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| Author(s) : Roberts MS , Macauley SL , Wong AM , Yilmas D , Hohm S , Cooper JD , Sands MS |
| Ref : J Inherit Metab Dis , 35 :847 , 2012 |
| Abstract : |
| PubMedSearch : Roberts_2012_J.Inherit.Metab.Dis_35_847 |
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| Ref : Hum Mol Genet , 18 :4066 , 2009 |
| Abstract : |
| PubMedSearch : Kielar_2009_Hum.Mol.Genet_18_4066 |
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| Ref : Experimental Neurology , 217 :124 , 2009 |
| Abstract : |
| PubMedSearch : Macauley_2009_Exp.Neurol_217_124 |
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| Title : Long-term clinical outcome after transcervical thymectomy for myasthenia gravis - Bril_1998_Ann.Thorac.Surg_65_1520 |
| Author(s) : Bril V , Kojic J , Ilse WK , Cooper JD |
| Ref : Annals of Thoracic surgery , 65 :1520 , 1998 |
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| Title : Absence of p75NTR causes increased basal forebrain cholinergic neuron size, choline acetyltransferase activity, and target innervation - Yeo_1997_J.Neurosci_17_7594 |
| Author(s) : Yeo TT , Chua-Couzens J , Butcher LL , Bredesen DE , Cooper JD , Valletta JS , Mobley WC , Longo FM |
| Ref : Journal of Neuroscience , 17 :7594 , 1997 |
| Abstract : |
| PubMedSearch : Yeo_1997_J.Neurosci_17_7594 |
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