| Title : Synergistic effects of treating the spinal cord and brain in CLN1 disease - Shyng_2017_Proc.Natl.Acad.Sci.U.S.A_114_E5920 |
| Author(s) : Shyng C , Nelvagal HR , Dearborn JT , Tyynela J , Schmidt RE , Sands MS , Cooper JD |
| Ref : Proc Natl Acad Sci U S A , 114 :E5920 , 2017 |
| Abstract : |
| PubMedSearch : Shyng_2017_Proc.Natl.Acad.Sci.U.S.A_114_E5920 |
| PubMedID: 28673981 |
| Gene_locus related to this paper: mouse-ppt |
| Title : Intrathecal enzyme replacement therapy improves motor function and survival in a preclinical mouse model of infantile neuronal ceroid lipofuscinosis - Lu_2015_Mol.Genet.Metab_116_98 |
| Author(s) : Lu JY , Nelvagal HR , Wang L , Birnbaum SG , Cooper JD , Hofmann SL |
| Ref : Mol Genet Metab , 116 :98 , 2015 |
| Abstract : |
| PubMedSearch : Lu_2015_Mol.Genet.Metab_116_98 |
| PubMedID: 25982063 |
| Gene_locus related to this paper: mouse-ppt |