Title : Intrathecal enzyme replacement therapy improves motor function and survival in a preclinical mouse model of infantile neuronal ceroid lipofuscinosis - Lu_2015_Mol.Genet.Metab_116_98 |
Author(s) : Lu JY , Nelvagal HR , Wang L , Birnbaum SG , Cooper JD , Hofmann SL |
Ref : Mol Genet Metab , 116 :98 , 2015 |
Abstract : Lu_2015_Mol.Genet.Metab_116_98 |
ESTHER : Lu_2015_Mol.Genet.Metab_116_98 |
PubMedSearch : Lu_2015_Mol.Genet.Metab_116_98 |
PubMedID: 25982063 |
Gene_locus related to this paper: mouse-ppt |
Gene_locus related to this paper: mouse-ppt |
Lu JY, Nelvagal HR, Wang L, Birnbaum SG, Cooper JD, Hofmann SL (2015)
Intrathecal enzyme replacement therapy improves motor function and survival in a preclinical mouse model of infantile neuronal ceroid lipofuscinosis
Mol Genet Metab
116 :98
Lu JY, Nelvagal HR, Wang L, Birnbaum SG, Cooper JD, Hofmann SL (2015)
Mol Genet Metab
116 :98