| Title : Gene therapy ameliorates bowel dysmotility and enteric neuron degeneration and extends survival in lysosomal storage disorder mouse models - Ziolkowska_2025_Sci.Transl.Med_17_eadj1445 |
| Author(s) : Ziolkowska EA , Jansen MJ , Williams LL , Wang SH , Eultgen EM , Takahashi K , Le SQ , Nelvagal HR , Sharma J , Sardiello M , DeBosch BJ , Dickson PI , Anderson JB , Sax SE , Wright CM , Bradley RP , Whiteman IT , Makita T , Grider JR , Sands MS , Heuckeroth RO , Cooper JD |
| Ref : Sci Transl Med , 17 :eadj1445 , 2025 |
| Abstract : |
| PubMedSearch : Ziolkowska_2025_Sci.Transl.Med_17_eadj1445 |
| PubMedID: 39813314 |
| Gene_locus related to this paper: mouse-ppt , human-PPT1 |
| Title : Gene therapy ameliorates bowel dysmotility and enteric neuron degeneration and extends survival in lysosomal storage disorder mouse models - Ziolkowska_2025_Sci.Transl.Med_17_eadj1445 |
| Author(s) : Ziolkowska EA , Jansen MJ , Williams LL , Wang SH , Eultgen EM , Takahashi K , Le SQ , Nelvagal HR , Sharma J , Sardiello M , DeBosch BJ , Dickson PI , Anderson JB , Sax SE , Wright CM , Bradley RP , Whiteman IT , Makita T , Grider JR , Sands MS , Heuckeroth RO , Cooper JD |
| Ref : Sci Transl Med , 17 :eadj1445 , 2025 |
| Abstract : |
| PubMedSearch : Ziolkowska_2025_Sci.Transl.Med_17_eadj1445 |
| PubMedID: 39813314 |
| Gene_locus related to this paper: mouse-ppt , human-PPT1 |
| Title : Gene therapy ameliorates bowel dysmotility and enteric neuron degeneration and extends survival in lysosomal storage disorder mouse models - Ziolkowska_2025_Sci.Transl.Med_17_eadj1445 |
| Author(s) : Ziolkowska EA , Jansen MJ , Williams LL , Wang SH , Eultgen EM , Takahashi K , Le SQ , Nelvagal HR , Sharma J , Sardiello M , DeBosch BJ , Dickson PI , Anderson JB , Sax SE , Wright CM , Bradley RP , Whiteman IT , Makita T , Grider JR , Sands MS , Heuckeroth RO , Cooper JD |
| Ref : Sci Transl Med , 17 :eadj1445 , 2025 |
| Abstract : |
| PubMedSearch : Ziolkowska_2025_Sci.Transl.Med_17_eadj1445 |
| PubMedID: 39813314 |
| Gene_locus related to this paper: mouse-ppt , human-PPT1 |
| Title : The timing and location of glial cell line-derived neurotrophic factor expression determine enteric nervous system structure and function - Wang_2010_J.Neurosci_30_1523 |
| Author(s) : Wang H , Hughes I , Planer W , Parsadanian A , Grider JR , Vohra BP , Keller-Peck C , Heuckeroth RO |
| Ref : Journal of Neuroscience , 30 :1523 , 2010 |
| Abstract : |
| PubMedSearch : Wang_2010_J.Neurosci_30_1523 |
| PubMedID: 20107080 |
| Title : The timing and location of glial cell line-derived neurotrophic factor expression determine enteric nervous system structure and function - Wang_2010_J.Neurosci_30_1523 |
| Author(s) : Wang H , Hughes I , Planer W , Parsadanian A , Grider JR , Vohra BP , Keller-Peck C , Heuckeroth RO |
| Ref : Journal of Neuroscience , 30 :1523 , 2010 |
| Abstract : |
| PubMedSearch : Wang_2010_J.Neurosci_30_1523 |
| PubMedID: 20107080 |
| Title : The timing and location of glial cell line-derived neurotrophic factor expression determine enteric nervous system structure and function - Wang_2010_J.Neurosci_30_1523 |
| Author(s) : Wang H , Hughes I , Planer W , Parsadanian A , Grider JR , Vohra BP , Keller-Peck C , Heuckeroth RO |
| Ref : Journal of Neuroscience , 30 :1523 , 2010 |
| Abstract : |
| PubMedSearch : Wang_2010_J.Neurosci_30_1523 |
| PubMedID: 20107080 |